United States
US 12,697,399 B2
Microdystrophin gene therapy constructs and uses thereof
US 12,697,399 B2 is a granted patent from the United States Patent and Trademark Office (USPTO), dated 2026-08-04. Applicant: REGENXBIO Inc. Its PDF downloads from this page without an account, up to 5 a day.
- Applicant
- REGENXBIO Inc.
- Inventors
- Chunping Qiao; Devin McDougald; Ye Liu; Olivier Danos
- Publication date
- 2026-08-04
- Filing date
- 2022-05-20
- Document type
- B2 Granted patent
- Also written as
- US 12,697,399 B2 · US12697399 · 12697399
Abstract
Provided are gene constructs that encode a microdystrophin protein for use in gene therapy. The microdystrophin gene constructs and expression cassettes were engineered for improved therapy with respect to efficacy, potency and safety to the subject when expressed by a viral vector in muscle cells and/or CNS cells.
The opening of the abstract. The full text is in the PDF.
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Patent office website: United States Patent and Trademark Office (USPTO)
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